Case Studies

The client wants to better understand and evaluate the ROI of potential patient engagement activities to initiate

Understanding the major players on the national or European level

The client needs to understand the needs, challenges, everyday life, preferences, and hopes for the future of families affected by a rare, genetic disease.

A client wishes to submit an HTA dossier to a payer institution for a therapeutic indication with many other approved treatments already existing on the market

The client needs to obtain the patient view and preferences on clinical trial design, especially in regard to the burden of the trial, in- and exclusion criteria and readability of consent material

The client needed assistance recruiting patients for a phase I/II trial in a disease area with many other simultaneously ongoing clinical trials

The client would like to establish a European patient advisory board to guide upcoming clinical trials, act as a sounding board to hear patient concerns firsthand and get regular advice from patient advocates on a variety of topics in R&D

A company is developing a new medical product for patients with a rare disease. Additional services, e.g. a patient-support-program (PSP), are considered important to help patients gaining access to new treatments when needed

In order for the European Medicines Agency to maintain the marketing authorization for mexiletine, data was necessary to evaluate the use and access to mexiletine across Europe.

There are a lot of impressive stories about how "the rare ones" deal with their daily challenges and find solutions. We want to introduce some of these people, share ideas, encourage and inspire.